Tag: Muscular dystrophy
FDA committee backs approval of Sarepta Therapeutics’ SRP-9001 for DMD
Sarepta Therapeutics’ SRP-9001 (delandistrogene moxeparvovec) has received the backing of the Cellular, Tissue and Gene Therapies Advisory Committee (CTGTAC) of the US Food and Drug ... Read More
PTC Therapeutics wins Russian approval for Translarna for nmDMD
US-based PTC Therapeutics has secured marketing approval in Russia for Translarna (ataluren) for the treatment of nonsense mutation Duchenne muscular dystrophy (nmDMD). The approval for ... Read More
Astellas Pharma to acquire US gene therapy company Audentes Therapeutics
Astellas acquisition of Audentes: Japanese pharma company Astellas Pharma has agreed to acquire US gene therapy company Audentes Therapeutics in an all-cash deal worth about ... Read More
What is Muscular Dystrophy and Types of Muscular Dystrophy Explained
DailyHealthNeeds.com brings you the basic introduction to Muscular Dystrophy in simple easy to understand language. Find out about Muscular Dystrophy causes, Muscular Dystrophy symptoms and ... Read More
Potential Duchenne Muscular Dystrophy therapy from Exonics gets $5m boost
US based Exonics Therapeutics has secured $5 million seed funding from CureDuchenne Ventures, a subsidiary of nonprofit DMD advocacy group, CureDuchenne to advance its therapy ... Read More
Pathological Conditions,Laboratory Tests and Clinical Procedures of Muscular System
Pathological conditions related to the muscular system are: Muscular dystrophy Polymyositis Muscular dystrophy: Muscular dystrophy is a group of inherited diseases characterized by progressive weakness ... Read More